Dose level response rates of mTOR inhibition in tuberous sclerosis complex (TSC) related subependymal giant cell astrocytoma (SEGA)

Weidman, D. (2015) Pediatric Blood and Cancer (Link to abstract)                        

* Therapeutic dose of mTOR inhibitor is effective in shrinking TSC related SEGAs. Doses less than 2.5 mg/m2 were insufficient to maintain response in this limited series.

Thalassaemia in children: from quality of care to quality of life

Amid A (2015) Archives of disease in childhood (Link to abstract)

Review article of pathophysiology and advances in clinical care and quality of life in patients with thalassaemia with a focus on developing countries and their resources